Phase 3 Aspire did not achieve the primary endpoint of change from Baseline in Bayley-4 cognitive raw score nor the key ...

By Christy Santhosh Sept 2 (Reuters) - Ultragenyx Pharmaceutical said on Wednesday its experimental drug for a rare genetic neurodevelopmental disorder did not meet the main goal in a late-stage trial ...

Ultragenyx said its experimental therapy for Angelman syndrome, a rare disease, showed no benefit compared to a sham treatment in a Phase 3 trial.

Add Yahoo as a preferred source to see more of our stories on Google. Actor Colin Farrell recently disclosed that his son, James, has Angelman syndrome, one of the driving factors behind Farrell's ...

Add Yahoo as a preferred source to see more of our stories on Google. The rare neurogenetic disorder affects 1 in 15,000 people For the first time, Colin Farrell has opened up his home and talked ...

Angelman syndrome is a rare neurodevelopmental disorder characterized by changes in brain structure, severe intellectual disability, impairments in speech, motor function, epilepsy, sleep, and unique ...

Actor Colin Farrell is launching a foundation to support people with intellectual disabilities, inspired by his son James, who has a rare neurological condition called Angelman syndrome. “I want the ...

Actor Colin Farrell and his ex-partner Kim Bordenave have been quite open about the condition that has afflicted their son, James Farrell, who has been diagnosed with Angelman Syndrome. News emerged ...