An expert discusses the current treatment landscape of Rett syndrome including the goals of treatment and implications for utilization management strategies with the disease. David Lieberman, MD, PhD: ...

The US Food and Drug Administration has approved Acadia Pharmaceuticals’ Daybue Stix (trofinetide), a dye and ...

Rare genetic disorder shuts off motor skills; mental acuity may still be there. May 9, 2012— -- For the first year of life, Chelsea Coenraads was a perfectly normal child, playing peek-a-boo and ...

What is Rett syndrome and why does it affect only girls? Rett syndrome is a rare neurological disorder that causes victims to regress intellectually, gradually robbing their ability to think and move.

In commemoration of Rett syndrome awareness month this October, Acadia Pharmaceuticals is launching an awareness campaign to shine a light on patients' journeys and show that each person living with ...

Credit: Acadia Pharmaceuticals. The approval was supported by data from the randomized, double-blind, placebo-controlled phase 3 LAVENDER study. The Food and Drug Administration (FDA) has approved ...

With strong 1-year returns and upside potential, Taysha Gene Therapies, Inc. (NASDAQ:TSHA) secures a spot on our list of the ...

Paige Nues provides her closing thoughts regarding the treatment management of Rett syndrome. Paige Nues: We have never felt more optimistic than [at] any time in the Rett syndrome’s history in terms ...

The investigational drug trofinetide showed modest benefit in girls and young women with Rett syndrome, the phase III LAVENDER study showed. After 12 weeks of treatment, significant differences in two ...

Taysha Gene Therapies (TSHA) is back in focus after its Rett syndrome program hit several milestones at once, including FDA Breakthrough Therapy Designation for TSHA-102 and encouraging REVEAL study ...

-- First and only approved therapy for Rett syndrome, a rare, neurodevelopmental disorder, which affects 6,000 to 9,000 patients in the U.S. 1 SAN DIEGO--(BUSINESS WIRE)--Acadia Pharmaceuticals Inc.

BENGALURU: Awareness about rare diseases can sometimes prevent serious conditions from being overlooked. One such condition is Rett Syndrome, a rare neurological disorder that many people aren’t ...