European Commission approval expands the indication of lomitapide in the European Union (EU) to include children 5 years of ...

Frost & Sullivan, a global consulting and market research firm, has forecast that China's rare disease drug market will ...

The family has urged the court to direct the Union Government to release the required funds without delay.

When a rare but deadly rodent-borne virus struck passengers on a cruise ship and seemed to be spreading, there were no ...

Call it a run-in with reality. OpenAI executive Maggie Hott has crossed the finish lines of two Ironman triathlons and 21 ...

Opus Genetics (IRD) rated Hold: valuation hinges on AAV gene therapy success. Track LCA5 Phase 3, 2026 data catalysts & ...

Texas added a new enzyme deficiency test to its newborn screening, increasing the total conditions screened to 60.

International momentum is evidenced by the 2026 symposium attracting participants from 73 countries, and highlighting OGM ...

On track to complete enrollment of MIST Phase 2b trial of AP01 in progressive pulmonary fibrosis (PPF) in mid-2026, with ...

Is KRYS a good stock to buy? We came across a bullish thesis on Krystal Biotech, Inc. on Investment Management Academy’s ...

Shionogi Announces FDA Approval of XOCOVA®, the First and Only Oral Option to Help Prevent COVID-19 Following Exposure ...

The appointment comes as ENYO advances preparations for a pivotal Phase 3 program of Vonafexor in Alport Syndrome, a rare ...